Exploring Novel Clinical Trial Designs for Gene-Based Therapies: Proceedings of a Workshop

"Speakers at the workshop discussed patient recruitment and selection for gene-based clinical trials, explored how the safety of new therapies is assessed, reviewed the challenges involving dose escalation, and spoke about ethical issues such as informed consent and the role of clinicians in recommending trials as options to their patients"--The National Academies of Sciences, Engineering, Medicine website (viewed September 17, 2020)